Product Catalog [{"id":"579","name":"Agamree","price":0,"sku":"Agamree (vamorolone)","brand":false,"position":1,"category":"Medicines\/Neurology\/Duchenne Muscular Dystrophy"},{"id":"432","name":"Amondys 45","price":1,"sku":"Amondys 45 (casimersen)","brand":"Sarepta Therapeutics","position":2,"category":"Medicines\/Neurology\/Duchenne Muscular Dystrophy"},{"id":"378","name":"Viltepso","price":2176.2,"sku":"Viltolarsen (viltolarsen)","brand":"NS Pharma","position":3,"category":"Medicines\/Neurology\/Duchenne Muscular Dystrophy"},{"id":"377","name":"Vyondys 53","price":2867.85,"sku":"Vyondys 53 (golodirsen)","brand":"Sarepta Therapeutics","position":4,"category":"Medicines\/Neurology\/Duchenne Muscular Dystrophy"},{"id":"318","name":"Exondys 51","price":18348,"sku":"Exondys 51 (eteplirsen)","brand":"Sarepta Therapeutics, Inc.","position":5,"category":"Medicines\/Neurology\/Duchenne Muscular Dystrophy"},{"id":"46","name":"Calcort","price":27.2,"sku":"Calcort (deflazacort)","brand":"Merrell Dow\/Henning","position":6,"category":"Medicines\/Neurology\/Duchenne Muscular Dystrophy"}]

Duchenne Muscular Dystrophy access options

Duchenne muscular dystrophy (DMD) is a genetic neuromuscular disorder characterised by progressive muscle weakness and wasting. It is caused by mutations in the dystrophin gene on the X-chromosome which result in an absence of the dystrophin protein, a protein that helps keep muscle cells intact. It is the most prevalent neuromuscular disorder, affecting up to 1 out of 3,600 male births worldwide. Symptoms usually appear during in early childhood, between the ages 3 and 5. The disease primarily affects boys, but can also affect girls as well, although this is quite rare. The standard therapy that can delay DMD progression is based on corticosteroids. The two mainly used in DMD are deflazacort and prednisone/prednisolone. 
  1. Exondys 51
    Exondys 51 (eteplirsen)
    Duchenne Muscular Dystrophy
  2. Vyondys 53
    Vyondys 53 (golodirsen)
    Duchenne Muscular Dystrophy
  3. Viltepso
    Viltepso (viltolarsen)
    Duchenne Muscular Dystrophy
  4. Amondys 45
    Amondys 45 (casimersen)
    Duchenne Muscular Dystrophy
    Price available on request
  5. Calcort
    Calcort (deflazacort)
    Duchenne Muscular Dystrophy
  6. Agamree
    Agamree (vamorolone)
    Duchenne Muscular Dystrophy
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