Vyndaqel (tafamidis) is a medicine indicated for the treatment of transthyretin amyloidosis in patients with stage 1 symptomatic polyneuropathy to delay peripheral neurologic impairment.

Tibsovo (ivosidenib) is an IDH1 inhibitor (targeted therapy) medication.

Enhertu (fam-trastuzumab deruxtecan-nxki) is an antibody-drug conjugate targeted therapy.

Chronic Lymphocytic Leukemia (CLL) is a slow-growing disease in which too many immature lymphocytes (white blood cells, which are cells of the immune system of the body) are found mostly in the blood and bone marrow.

Muscular Dystrophy (MD) refers to a group of over 30 inherited genetic and progressive diseases caused by a mutation in a person’s genes. The different types of MD vary in signs, symptoms and affect specific muscle groups.

Acute myeloid leukemia (AML) also known as acute myelocytic leukemia, acute myelogenous leukemia, acute granulocytic leukemia, and acute non-lymphocytic leukemia.

Lung cancer begins in the lungs and may spread to lymph nodes or other organs in the body. Lung cancers usually are grouped into two main types:small cell and non-small cell.

Ovarian cancer forms in the tissues of the ovaries, the female reproductive glands. Ovaries are made up of 3 main kinds of cells: cells that cover the outer surface of the ovary, germ cells that produce the eggs, and cells that hold the ovary together and produce the female hormones estrogen and progesterone.

A migraine is a moderate to severe headache described as a beating pain on one side of the head. It can be accompanied by other symptoms, including sensitivity to sounds and light, or feeling sick (nausea, vomiting).

Pseudobulbar Affect (PBA) is a neurological condition that causes outbursts of uncontrolled or inappropriate laughing or crying. It is also known by other names including emotional lability, pathological laughing and crying, involuntary emotional expression disorder, compulsive laughing or weeping, or emotional incontinence.

Renal cell carcinoma (RCC) also called kidney cancer or renal cell cancer is a disease in which malignant cancer cells are found in the lining of tubules in the kidney. RCC accounts for more than 80% of all kidney cancers.

Rheumatoid arthritis (RA) is an autoimmune disease where the immune system attacks body tissues. It primarily affects joints, but it can also cause inflammation of organs, such as the lungs, eyes, skin, and heart.

Multiple Sclerosis (MS) is a chronic, inflammatory, autoimmune disease of the central nervous system that disrupts communication between the brain and other parts of the body.

Parkinson’s disease (PD) is a progressive brain disorder that causes shaking and muscle stiffness, and slows movement.

Colorectal cancer or colon cancer is cancer of the large intestine (colon), which is the final part of the digestive tract. Both colon cancer and rectal cancer can be referred to as colorectal or bowel cancer, but there is a slight difference between the two based on where the cancer begins.

There are several ALS medications that are not yet approved in any country and currently under clinical trial. Read about the latest approved treatments.

Human epidermal growth factor receptor 2 (HER2) is a growth-promoting protein on the outside of all breast cells. Breast cancer cells with higher than normal levels of HER2 are called HER2-positive.

Triple-negative breast cancer (TNBC) is a cancer that tests negative for progesterone and estrogen receptors, and excess HER2 protein. This means that the growth of the cancer is not fuelled by the estrogen and progesterone hormones, or by the HER2 protein. So, TNBC does not respond to hormonal therapy medicines or medicines that target HER2 protein receptors.

Aimovig (erenumab) is a preventive migraine treatment that works by blocking the activity of calcitonin gene-related peptide, a molecule that is involved in migraine attacks

Here is an overview of each medicine to help guide you and your physician when making a treatment decision for Cystic Fibrosis: 

Marcus was diagnosed with amyotrophic lateral sclerosis (ALS) in 2016. For the past four years he has been committed to raising awareness about the underfunded disease and the path to finding a cure.

Our logistics team is responsible for delivering medicines to patients anywhere they may be. Every medicine is treated with extra care to ensure its safe and timely delivery.

When our patients submit an inquiry for a medicine, they are then personally contacted by one of our Patient Support team members who assist them through the entire process of ordering, sourcing and delivering their medicines.

Here are some frequently asked questions and answers that touch on important COVID-19 related updates.

After submitting a request and receiving a quote from our Patient Support Team, patients often have many questions regarding the price that they receive. In this article, you can find a breakdown of the total cost of a medicine we are supporting you to access in addition to resources on how you can possibly get it reimbursed.

In order to help you expedite the request process with us, we put together a quick prescription guideline.

5 common questions about the supplement that may be useful for ALS, Parkinson's and Alzheimers.

New analysis of Biogen’s aducanumab shows reduction in clinical decline in Alzheimer’s disease.

As a pioneer of a completely new type of global service, we understand that trust, security and credibility are paramount–especially when paying for medicines which are essential and often the only treatment option available. There are an increasing number of scam websites and we ourselves have been the subject of one such scam. In this article we’ll give you tips on how to spot these fakers.

I’m lucky. It's been 4 years since the first MND symptoms, only my voice has been impacted.