Over 50 countries have approved Spinraza (nusinersen), but not all have made it available to the patients who need it.
spinal muscular atrophy
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January 18, 2019Read more »
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December 14, 2018Read more »
Zolgensma (onasemnogene abeparvovec-xxxx) to receive priority review by FDA as a one-time treatment of type 1 spinal muscular atrophy (SMA).
